Cells for medical or clinical use; pharmaceutical and biopharmaceutical agents for the treatment of Sickle cell disease and B-thalassemi; pharmaceutical products and preparations, namely, gene transfer, regulation, modulation and delivery pharmaceuticals for the treatment of genetic diseases and disorders

'agent':10 'b':20 'b-thalassemi':19 'biopharmaceut':9 'cell':1,16 'clinic':5 'deliveri':32 'diseas':17,39 'disord':41 'gene':27 'genet':38 'medic':3 'modul':30 'name':26 'pharmaceut':7,22,33 'prepar':25 'product':23 'regul':29 'sickl':15 'thalassemi':21 'transfer':28 'treatment':13,36 'use':6

CTX001

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